|
1
|
Moscioni D, Morizono H, McCarter R, et al:
Long-term correction of ammonia metabolism and prolonged survival
in ornithine transcarbamylase-deficient mice following
liver-directed treatment with adeno-associated viral vectors. Mol
Ther. 14:25–33. 2006. View Article : Google Scholar
|
|
2
|
Hauswirth WW, Aleman TS, Kaushal S, et al:
Treatment of leber congenital amaurosis due to RPE65 mutations by
ccular subretinal injection of adeno-associated virus gene vector:
short-term results of a phase I trial. Hum Gene Ther. 19:979–990.
2008. View Article : Google Scholar : PubMed/NCBI
|
|
3
|
Manno CS, Chew AJ, Hutchison S, et al:
AAV-mediated factor IX gene transfer to skeletal muscle in patients
with severe hemophilia B. Blood. 101:2963–2972. 2003. View Article : Google Scholar : PubMed/NCBI
|
|
4
|
Kaplitt MG, Feigin A, Tang C, et al:
Safety and tolerability of gene therapy with an adeno-associated
virus (AAV) borne GAD gene for Parkinson's disease: an open label,
phase I trial. Lancet. 369:2097–2105. 2007. View Article : Google Scholar : PubMed/NCBI
|
|
5
|
Brantly ML, Spencer LT, Humphries M, et
al: Phase I trial of intramuscular injection of a recombinant
adeno-associated virus serotype 2 alphal-antitrypsin (AAT) vector
in AAT-deficient adults. Hum Gene Ther. 17:1177–1186. 2006.
View Article : Google Scholar : PubMed/NCBI
|
|
6
|
Bartlett JS, Kleinschmidt J, Boucher RC
and Samulski RJ: Targeted adeno-associated virus vector
transduction of nonpermissive cells mediated by a bispecific
F(ab'gamma)2 antibody. Nat Biotechnol. 17:181–186. 1999. View Article : Google Scholar : PubMed/NCBI
|
|
7
|
Hansen J, Qing K and Srivastava A:
Infection of purified nuclei by adeno-associated virus 2. Mol Ther.
4:289–296. 2001. View Article : Google Scholar : PubMed/NCBI
|
|
8
|
Takahashi K and Yamanaka S: Induction of
pluripotent stem cells from mouse embryonic and adult fibroblast
cultures by defined factors. Cell. 126:663–676. 2006. View Article : Google Scholar : PubMed/NCBI
|
|
9
|
Robinton DA and Daley GQ: The promise of
induced pluripotent stem cells in research and therapy. Nature.
481:295–305. 2012. View Article : Google Scholar : PubMed/NCBI
|
|
10
|
Hansen J, Qing K and Srivastava A:
Adeno-associated virus type 2-mediated gene transfer: altered
endocytic processing enhances transduction efficiency in murine
fibroblasts. J Virol. 75:4080–4090. 2001. View Article : Google Scholar
|
|
11
|
Hansen J, Qing K, Kwon HJ, Mah C and
Srivastava A: Impaired intracellular trafficking of
adeno-associated virus type 2 vectors limits efficient transduction
of murine fibroblasts. J Virol. 74:992–996. 2000. View Article : Google Scholar
|
|
12
|
Müller OJ, Schinkel S, Kleinschmidt JA,
Katus HA and Bekeredjian R: Augmentation of AAV-mediated cardiac
gene transfer after systemic administration in adult rats. Gene
Ther. 15:1558–1565. 2008.PubMed/NCBI
|
|
13
|
Li HL, Zheng XZ, Wang HP, Li F, Wu Y and
Du LF: Ultrasound-targeted microbubble destruction enhances
AAV-mediated gene transfection in human RPE cells in vitro and rat
retina in vivo. Gene Ther. 16:1146–1153. 2009. View Article : Google Scholar : PubMed/NCBI
|
|
14
|
Xie W, Liu S, Su H, Wang Z, Zheng Y and Fu
Y: Ultrasound microbubbles enhance recombinant adeno-associated
virus vector delivery to retinal ganglion cells in vivo. Acad
Radiol. 17:1242–1248. 2010. View Article : Google Scholar : PubMed/NCBI
|
|
15
|
Zheng X, Du L, Wang H and Gu Q: A novel
approach to attenuate proliferative vitreoretinopathy using
ultrasound-targeted microbubble destruction and recombinant
adeno-associated virus-mediated RNA interference targeting
transforming growth factor-β2 and platelet-derived growth factor-B.
J Gene Med. 14:339–347. 2012.PubMed/NCBI
|
|
16
|
Mehier-Humbert S, Bettinger T, Yan F and
Guy RH: Plasma membrane poration induced by ultrasound exposure:
implication for drug delivery. J Control Release. 104:213–222.
2005. View Article : Google Scholar : PubMed/NCBI
|
|
17
|
van Wamel A, Kooiman K, Harteveld M, et
al: Vibrating microbubbles poking individual cells: drug transfer
into cells via sonoporation. J Control Release. 112:149–155.
2006.PubMed/NCBI
|
|
18
|
Taniyama Y, Tachibana K, Hiraoka K, et al:
Local delivery of plasmid DNA into rat carotid artery using
ultrasound. Circulation. 105:1233–1239. 2002. View Article : Google Scholar : PubMed/NCBI
|
|
19
|
Suzuki R, Oda Y, Utoguchi N and Maruyama
K: Progress in the development of ultrasound-mediated gene delivery
systems utilizing nano- and microbubbles. J Control Release.
149:36–41. 2011. View Article : Google Scholar : PubMed/NCBI
|
|
20
|
Meijering BD, Juffermans LJ, van Wamel A,
et al: Ultrasound and microbubble-targeted delivery of
macromolecules is regulated by induction of endocytosis and pore
formation. Circ Res. 104:679–687. 2009. View Article : Google Scholar : PubMed/NCBI
|
|
21
|
Hauser J, Ellisman M, Steinau HU, Stefan
E, Dudda M and Hauser M: Ultrasound enhanced endocytotic activity
of human fibroblasts. Ultrasound Med Biol. 35:2084–2092. 2009.
View Article : Google Scholar : PubMed/NCBI
|
|
22
|
Lionetti V, Fittipaldi A, Agostini S,
Giacca M, Recchia FA and Picano E: Enhanced caveolae-mediated
endocytosis by diagnostic ultrasound in vitro. Ultrasound Med Biol.
35:136–143. 2009. View Article : Google Scholar : PubMed/NCBI
|
|
23
|
Paula DM, Valero-Lapchik VB,
Paredes-Gamero EJ and Han SW: Therapeutic ultrasound promotes
plasmid DNA uptake by clathrin-mediated endocytosis. J Gene Med.
13:392–401. 2011. View
Article : Google Scholar : PubMed/NCBI
|
|
24
|
Zhong L, Zhao W, Wu J, Maina N, Han Z and
Srivastava A: Adeno-associated virus-mediated gene transfer in
hematopoietic stem/progenitor cells as a therapeutic tool. Curr
Gene Ther. 6:683–698. 2006. View Article : Google Scholar : PubMed/NCBI
|
|
25
|
Stender S, Murphy M, O'Brien T, et al:
Adeno-associated viral vector transduction of human mesenchymal
stem cells. Eur Cell Mater. 13:93–99. 2007.PubMed/NCBI
|
|
26
|
Li M, Jayandharan GR, Li B, et al:
High-efficiency transduction of fibroblasts and mesenchymal stem
cells by tyrosine-mutant AAV2 vectors for their potential use in
cellular therapy. Human Gene Ther. 21:1527–1543. 2010. View Article : Google Scholar : PubMed/NCBI
|
|
27
|
Duan D, Yue Y, Yan Z, Yang J and
Engelhardt JF: Endosomal processing limits gene transfer to
polarized airway epithelia by adeno-associated virus. J Clin
Invest. 105:1573–1587. 2000. View
Article : Google Scholar : PubMed/NCBI
|
|
28
|
Qing K, Hansen J, Weigel-Kelley KA, Tan M,
Zhou S and Srivastava A: Adeno-associated virus type 2-mediated
gene transfer: role of cellular FKBP52 protein in transgene
expression. J Virol. 75:8968–8976. 2001. View Article : Google Scholar : PubMed/NCBI
|
|
29
|
Qing K, Mah C, Hansen J, Zhou S, Dwarki V
and Srivastava A: Human fibroblast growth factor receptor 1 is a
co-receptor for infection by adeno-associated virus 2. Nat Med.
5:71–77. 1999. View
Article : Google Scholar : PubMed/NCBI
|
|
30
|
Ponnazhagan S, Wang XS, Woody MJ, et al:
Differential expression in human cells from the p6 promoter of
human parvovirus B19 following plasmid transfection and recombinant
adeno-associated virus 2 (AAV) infection: human megakaryocytic
leukaemia cells are non-permissive for AAV infection. J Gen Virol.
77:1111–1122. 1996. View Article : Google Scholar
|
|
31
|
Xie W, Liu S, Su H, Wang Z, Zheng Y and Fu
Y: Ultrasound microbubbles enhance recombinant adeno-associated
virus vector delivery to retinal ganglion cells in vivo. Acad
Radiol. 17:1242–1248. 2010. View Article : Google Scholar : PubMed/NCBI
|
|
32
|
Stride E and Saffari N: Investigating the
significance of multiple scattering in ultrasound contrast agent
particle populations. IEEE Trans Ultrason Ferroelectr Freq Control.
52:2332–2345. 2005. View Article : Google Scholar : PubMed/NCBI
|
